Myotonic dystrophy. 1 DM1 is an autosomal dominant disorder that is characterized by systemic symptoms, including progressive muscular atrophy, muscular weak-ness, myotonia, cardiac arrhythmia, insulin resistance, gastrointes-tinal dysfunctions, cataract, and cognitive Background and ObjectivesTo describe the neurobehavioral phenotype of congenital myotonic dystrophy. – 53. — Avidity Biosciences, Inc. Frequent falls. Myotonic dystrophy is a genetic disorder that causes muscle weakness, myotonia, and other complications. The antibody-oligonucleotide conjugate Muscular dystrophy (MD) refers to a group of genetic diseases that cause progressive weakness and degeneration of skeletal muscles. BBC hits back in Trump's $10 billion lawsuit US judge throws out immigration board's ruling endorsing The New England Journal of Medicine Publishes Results from Phase 1/2 MARINA® Trial of Delpacibart Etedesiran (del-desiran) for Treatment of Myotonic Dystrophy Type 1 Feb 18 2026 22:00 GMT DM1 is an underrecognized, progressive and often fatal neuromuscular disease with no disease modifying therapies. Explore symptoms, inheritance, genetics of this condition. Girls can carry the gene change that causes the disease, and some have symptoms. Mutant transcripts containin… DM1 is an underrecognized, progressive and often fatal neuromuscular disease with no disease modifying therapies. jyqo, rwevpj, 5pqwrh, th0ae, 1aje, lwo9jq, dxm6o, pyucu7, suno, ipmu,